Better Health, Brighter Future

The drive to become a leading biotech company focused on innovative approaches to treat rare and specialty diseases, shapes the foundation of our Research and Development approach. Our expertise in discovering new therapies for rare, life-threatening genetic diseases as well as in developing medicines for patients treated by specialist physicians, demonstrates our continued commitment to patients and their caregivers.

For more information on Research and Development, including on-going clinical trials, please visit our global website here.

For more information on ongoing Canadian clinical trials, please visit the Health Canada clinical trial database available here.

In This Section

We strive for operational excellence in a wide range of clinical studies.


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